Bow Foundation 2025 Grant Program - Letter of Interest

Ends on

The Bow Foundation will provide a 1-year grant to support research related to GNAO1

Neurodevelopmental Disorder. At least 2 awards will be granted at $100,000 each.

Background

GNAO1 (G Protein Subunit Alpha O1) is a protein coding gene. Most patients with a GNAO1

neurodevelopmental disorder are diagnosed as infants or young children. Many of the patients begin

experiencing seizures, abnormal movements and developmental delays in their infancy. The

seizures are often refractory, and the patients seem to cycle through numerous medications as they

try to find relief. The abnormal movements seem to worsen as the patients age. Several patients have

benefited from deep brain stimulation surgery, including the youngest patient in the world to receive

the procedure (a 2-year-old in the UK).

The Orphan Disease Center, in collaboration with the Bow Foundation, is seeking grant applications

that aim to further progress our understanding of the disease, the available therapeutic options, and

investigating strategies to establish outcome measurements. The RFA could focus on one, or several,

of the following aims, to further advance GNAO1 research and therapeutic approaches:

  • Novel therapeutic approaches, including, but not limited to, techniques in genome editing,

RNA-based mechanisms, biologics, novel cell-based therapeutics, and development of novel

therapeutic compounds, including through small molecule repurposing or screening against

validated phenotypes in human cellular systems.

  • Proposals that include collaboration across organizations or other rare diseases.
  • Establishment of outcome measures for future clinical trials.
  •  Supporting pilot clinical trials, preclinical trials, or animal model trials that promote drug

repurposing strategies.

  • Other aims are welcome and will be considered.


Eligibility

All individuals holding a faculty-level appointment at an academic institution or a senior position at a

non-profit institution or foundation are eligible to respond to this RFA.

We use Submittable to accept and review our submissions.